Management of CLN1 Disease: International Clinical Consensus

Erika F. Augustine, Heather R. Adams, Emily de los Reyes, Kristen Drago, Margie Frazier, Norberto Guelbert, Minna Laine, Tanya Levin, Jonathan W. Mink, Miriam Nickel, Danielle Peifer, Angela Schulz, Alessandro Simonati, Meral Topcu, Joni A. Turunen, Ruth Williams, Elaine C. Wirrell, Sharon King

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