Enzyme replacement therapy results in substantial improvements in early clinical phenotype in a mouse model of globoid cell leukodystrophy

Wing C. Lee, Andrew Courtenay, Frederick J. Troendle, Melody L. Stallings-Mann, Chad A. Dickey, Michael W. DeLucia, Dennis W. Dickson, Christopher B. Eckman

Research output: Contribution to journalArticlepeer-review

69 Scopus citations
Original languageEnglish (US)
Pages (from-to)1549-1551
Number of pages3
JournalFASEB Journal
Issue number11
StatePublished - Sep 2005

ASJC Scopus subject areas

  • Biotechnology
  • Biochemistry
  • Molecular Biology
  • Genetics

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