The ISIS-TTRRx-CS2 phase 3 study in patients with familial amyloid polyneuropathy: Baseline results of the first 100 patients for the NIS, NIS+7 and mNIS+7 using different methods of scoring: identification of consistencies and key differences

Rito Bergemann, Elizabeth Ackermann, Brett Monia, Andrew Shenker, Peter Dyck

Research output: Contribution to journalArticlepeer-review

Original languageEnglish (US)
Pages (from-to)1-2
Number of pages2
JournalOrphanet Journal of Rare Diseases
StatePublished - 2015

ASJC Scopus subject areas

  • Genetics(clinical)
  • Pharmacology (medical)

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